Seven Diseases could be Cured by CRISPR-Cas9: A Revolutionary Technology of Gene editing.

Seven Diseases could be Cured by CRISPR-Cas9: A Revolutionary Technology of Gene editing.

CRISPR technology offers the promise to cure any human genetic disease.

Which are the candidates to be the first one?

CRISPR-Cas9 was first used as a gene editing tool in 2012.

In just a few years, the technology has exploded in popularity thanks to its promise of making gene editing much faster, cheaper and easier than ever before.

CRISPR has already changed the way scientists do research.

But what everyone is expecting, either with excitement or fear, is its use in humans specially off target effects!

In theory, CRISPR technology could let us edit any genetic mutation at will, curing the disease it causes.

In practice, it is just the beginning of the development of CRISPR as a therapy and there are still many unknowns.

Thus an attempt has been made in this E-Booklet to include the seven diseases that scientists are already tackling with the help of CRISPR-Cas9, and which could eventually become the first conditions to ever be treated with this revolutionary technology.

Blood Disorders
Cancer
Blindness
AIDS
Muscular dystrophy
Huntington's disease
Cystic fibrosis

Dr. H. K. Saboowala.

M.B.(Bom)M.R.S.H.(London)

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